Human liver chimeric mice as a new model of chronic hepatitis E virus infection and preclinical drug evaluation

J Hepatol. 2016 May;64(5):1033-1040. doi: 10.1016/j.jhep.2016.01.011. Epub 2016 Jan 22.

Abstract

Background & aims: Hepatitis E virus (HEV) is a major cause of acute hepatitis as well as chronic infection in immunocompromised individuals; however, in vivo infection models are limited. The aim of this study was to establish a small animal model to improve our understanding of HEV replication mechanisms and permit the development of effective therapeutics.

Methods: UPA/SCID/beige mice repopulated with primary human hepatocytes were used for infection experiments with HEV genotype (GT) 1 and 3. Virological parameters were determined at the serological and intrahepatic level by real time PCR, immunohistochemistry and RNA in situ hybridization.

Results: Establishment of HEV infection was achieved after intravenous injection of stool-derived virions and following co-housing with HEV-infected animals but not via inoculation of serum-derived HEV. GT 1 infection resulted in a rapid rise of viremia and high stable titres in serum, liver, bile and faeces of infected mice for more than 25 weeks. In contrast, viremia in GT 3 infected mice developed more slowly and displayed lower titres in all analysed tissues as compared to GT 1. HEV-infected human hepatocytes could be visualized using HEV ORF2 and ORF3 specific antibodies and HEV RNA in situ hybridization probes. Finally, six-week administration of ribavirin led to a strong reduction of viral replication in the serum and liver of GT 1 infected mice.

Conclusion: We established an efficient model of HEV infection to test the efficacy of antiviral agents and to exploit mechanisms of HEV replication and interaction with human hepatocytes in vivo.

Keywords: Chronic viral hepatitis; Hepatitis E Virus (HEV); Humanized mice; Preclinical drug testing; Ribavirin; uPA/SCID/beige.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Antiviral Agents / therapeutic use*
  • Disease Models, Animal
  • Drug Evaluation, Preclinical
  • Hepatitis E / drug therapy*
  • Hepatitis E / virology
  • Hepatitis E virus / genetics*
  • Humans
  • In Situ Hybridization
  • Liver / pathology
  • Liver / virology*
  • Mice
  • Mice, SCID
  • RNA, Viral / analysis*
  • Real-Time Polymerase Chain Reaction
  • Virus Replication / drug effects*

Substances

  • Antiviral Agents
  • RNA, Viral