β1-Na(+),K(+)-ATPase gene therapy upregulates tight junctions to rescue lipopolysaccharide-induced acute lung injury

Gene Ther. 2016 Jun;23(6):489-99. doi: 10.1038/gt.2016.19. Epub 2016 Mar 17.

Abstract

Acute lung injury (ALI) and acute respiratory distress syndrome (ARDS) are associated with diverse disorders and characterized by disruption of the alveolar-capillary barrier, leakage of edema fluid into the lung, and substantial inflammation leading to acute respiratory failure. Gene therapy is a potentially powerful approach to treat ALI/ARDS through repair of alveolar epithelial function. Herein, we show that delivery of a plasmid expressing β1-subunit of the Na(+),K(+)-ATPase (β1-Na(+),K(+)-ATPase) alone or in combination with epithelial sodium channel (ENaC) α1-subunit using electroporation not only protected from subsequent lipopolysaccharide (LPS)-mediated lung injury, but also treated injured lungs. However, transfer of α1-subunit of ENaC (α1-ENaC) alone only provided protection benefit rather than treatment benefit although alveolar fluid clearance had been remarkably enhanced. Gene transfer of β1-Na(+),K(+)-ATPase, but not α1-ENaC, not only enhanced expression of tight junction protein zona occludins-1 (ZO-1) and occludin both in cultured cells and in mouse lungs, but also reduced pre-existing increase of lung permeability in vivo. These results demonstrate that gene transfer of β1-Na(+),K(+)-ATPase upregulates tight junction formation and therefore treats lungs with existing injury, whereas delivery of α1-ENaC only maintains pre-existing tight junction but not for generation. This indicates that the restoration of epithelial/endothelial barrier function may provide better treatment of ALI/ARDS.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Acute Lung Injury / chemically induced
  • Acute Lung Injury / enzymology
  • Acute Lung Injury / genetics*
  • Acute Lung Injury / therapy*
  • Animals
  • Disease Models, Animal
  • Electroporation / methods
  • Epithelial Sodium Channels / therapeutic use
  • Genetic Therapy / methods*
  • Lipopolysaccharides
  • Male
  • Mice
  • Mice, Inbred C57BL
  • Plasmids / administration & dosage
  • Plasmids / genetics
  • Respiratory Distress Syndrome / therapy
  • Sodium-Potassium-Exchanging ATPase / administration & dosage
  • Sodium-Potassium-Exchanging ATPase / genetics*
  • Tight Junctions / enzymology
  • Tight Junctions / genetics
  • Tight Junctions / metabolism*
  • Up-Regulation

Substances

  • Epithelial Sodium Channels
  • Lipopolysaccharides
  • Sodium-Potassium-Exchanging ATPase