The first Japanese case of leukodystrophy with ovarian failure arising from novel compound heterozygous AARS2 mutations

J Hum Genet. 2016 Oct;61(10):899-902. doi: 10.1038/jhg.2016.64. Epub 2016 Jun 2.

Abstract

Even now, only a portion of leukodystrophy patients are correctly diagnosed, though various causative genes have been identified. In the present report, we describe a case of adult-onset leukodystrophy in a woman with ovarian failure. By whole-exome sequencing, a compound heterozygous mutation consisting of NM_020745.3 (AARS2_v001):c.1145C>A and NM_020745.3 (AARS2_v001):c.2255+1G>A was identified. Neither of the mutations has been previously reported, and this is the first report of alanyl-transfer RNA synthetase 2 mutation in Asia. We anticipate that further studies of the molecular basis of leukodystrophy will provide insight into its pathogenesis and hopefully lead to sophisticated diagnostic and treatment strategies.

Publication types

  • Case Reports

MeSH terms

  • Adult
  • Alanine-tRNA Ligase / genetics*
  • Alleles
  • Biomarkers
  • Brain / pathology
  • DNA Mutational Analysis
  • Female
  • Genetic Loci
  • Hereditary Central Nervous System Demyelinating Diseases / diagnosis
  • Hereditary Central Nervous System Demyelinating Diseases / genetics*
  • Heterozygote*
  • Humans
  • Japan
  • Magnetic Resonance Imaging
  • Mutation*
  • Primary Ovarian Insufficiency / diagnosis
  • Primary Ovarian Insufficiency / genetics*
  • Syndrome

Substances

  • Biomarkers
  • Alanine-tRNA Ligase