Abnormal processing of beta-Malay globin RNA

Biochem Biophys Res Commun. 1989 Aug 30;163(1):8-13. doi: 10.1016/0006-291x(89)92090-1.

Abstract

Hemoglobin Malay (alpha 2 beta 2 19 Asn----Ser) has been observed in a few Malaysian patients with thalassemia intermedia. The beta Malay substitution increases the homology of the cryptic splice site at codons 17/18/19 of the beta-globin gene to the donor consensus splice sequence, suggesting that the beta-thalassemia associated with this mutation may be due to the generation of a new splice site. To test this hypothesis, we constructed a hybrid gene where we replaced part of a normal beta-globin gene with a PCR amplified region of the beta Malay gene. The expression of this mutant gene was studied in a heterologous transient expression system. The data show that nearly 25% of globin mRNA produced by this gene is abnormally spliced at the new splice site, providing a molecular mechanism for the beta-thalassemia associated with the mutation.

Publication types

  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Base Sequence
  • Gene Amplification
  • Globins / genetics*
  • HeLa Cells
  • Hemoglobins, Abnormal / genetics*
  • Humans
  • In Vitro Techniques
  • RNA Processing, Post-Transcriptional*
  • RNA, Messenger / genetics
  • Thalassemia / genetics*
  • Transfection

Substances

  • Hemoglobins, Abnormal
  • RNA, Messenger
  • Globins