The long story of camptothecin: From traditional medicine to drugs

Bioorg Med Chem Lett. 2017 Feb 15;27(4):701-707. doi: 10.1016/j.bmcl.2016.12.085. Epub 2016 Dec 31.

Abstract

20-(S)-Camptothecin (CPT) is a natural alkaloid extracted from the bark of Camptotheca acuminata (Chinese happy tree). It acts as a DNA topoisomerase 1 poison with an interesting antitumor activity and its use is limited by low stability and solubility and unpredictable drug-drug interactions. Since the late 20th century, it has been widely used in cancer therapy and, since extraction yields from plant tissues are very low, various synthetic routes have been developed to satisfy the increase in demand for CPT. Moreover, SAR studies have allowed for the development of more potent CPT analogues topotecan and irinotecan. Unfortunately, resistance has already occurred in several tumour lines. Additional studies are needed to better understand the relationship between substituents and resistance, its clinical relevance and the impact of related gene polymorphism. One of the latest research approaches focuses on modifying the delivery mode to improve tumour cell uptake and reduce toxicity.

Keywords: Anticancer drugs; CPT-like compounds; Camptotheca acuminata; Camptothecin; DNA topoisomerase 1; Drug-resistance; Formulative studies.

Publication types

  • Review

MeSH terms

  • Antineoplastic Agents, Phytogenic / chemistry*
  • Antineoplastic Agents, Phytogenic / therapeutic use
  • Antineoplastic Agents, Phytogenic / toxicity
  • Apoptosis / drug effects
  • Camptotheca / chemistry
  • Camptotheca / metabolism
  • Camptothecin / analogs & derivatives*
  • Camptothecin / therapeutic use
  • Camptothecin / toxicity
  • DNA Topoisomerases, Type I / chemistry
  • DNA Topoisomerases, Type I / metabolism
  • Humans
  • Medicine, Traditional*
  • Neoplasms / drug therapy
  • Structure-Activity Relationship

Substances

  • Antineoplastic Agents, Phytogenic
  • DNA Topoisomerases, Type I
  • Camptothecin