Unifying mechanism for different fibrotic diseases

Proc Natl Acad Sci U S A. 2017 May 2;114(18):4757-4762. doi: 10.1073/pnas.1621375114. Epub 2017 Apr 19.

Abstract

Fibrotic diseases are not well-understood. They represent a number of different diseases that are characterized by the development of severe organ fibrosis without any obvious cause, such as the devastating diseases idiopathic pulmonary fibrosis (IPF) and scleroderma. These diseases have a poor prognosis comparable with endstage cancer and are uncurable. Given the phenotypic differences, it was assumed that the different fibrotic diseases also have different pathomechanisms. Here, we demonstrate that many endstage fibrotic diseases, including IPF; scleroderma; myelofibrosis; kidney-, pancreas-, and heart-fibrosis; and nonalcoholic steatohepatosis converge in the activation of the AP1 transcription factor c-JUN in the pathologic fibroblasts. Expression of the related AP1 transcription factor FRA2 was restricted to pulmonary artery hypertension. Induction of c-Jun in mice was sufficient to induce severe fibrosis in multiple organs and steatohepatosis, which was dependent on sustained c-Jun expression. Single cell mass cytometry revealed that c-Jun activates multiple signaling pathways in mice, including pAkt and CD47, which were also induced in human disease. αCD47 antibody treatment and VEGF or PI3K inhibition reversed various organ c-Jun-mediated fibroses in vivo. These data suggest that c-JUN is a central molecular mediator of most fibrotic conditions.

Keywords: anti-CD47 antibody therapy; c-JUN; fibrotic disease; scleroderma; signaling pathways.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, Non-P.H.S.
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Fos-Related Antigen-2 / genetics
  • Fos-Related Antigen-2 / metabolism
  • Humans
  • Idiopathic Pulmonary Fibrosis* / genetics
  • Idiopathic Pulmonary Fibrosis* / metabolism
  • Primary Myelofibrosis* / genetics
  • Primary Myelofibrosis* / metabolism
  • Proto-Oncogene Proteins c-jun* / genetics
  • Proto-Oncogene Proteins c-jun* / metabolism
  • Scleroderma, Systemic* / genetics
  • Scleroderma, Systemic* / metabolism
  • Transcription Factor AP-1* / genetics
  • Transcription Factor AP-1* / metabolism

Substances

  • FOSL2 protein, human
  • Fos-Related Antigen-2
  • Proto-Oncogene Proteins c-jun
  • Transcription Factor AP-1