Whole-genome sequencing revealed novel prognostic biomarkers and promising targets for therapy of ovarian clear cell carcinoma

Br J Cancer. 2017 Aug 22;117(5):717-724. doi: 10.1038/bjc.2017.228. Epub 2017 Jul 20.

Abstract

Background: Ovarian clear cell carcinoma (OCCC) is mostly resistant to standard chemotherapy that results in poor patient survival. To understand the genetic background of these tumours, we performed whole-genome sequencing of OCCC tumours.

Methods: Tumour tissue samples and matched blood samples were obtained from 55 Japanese women diagnosed with OCCC. Whole-genome sequencing was performed using the Illumina HiSeq platform according to standard protocols.

Results: Alterations to the switch/sucrose non-fermentable (SWI/SNF) subunit, the phosphatidylinositol-3-kinase (PI3K)/Akt signalling pathway, and the receptor tyrosine kinase (RTK)/Ras signalling pathway were found in 51%, 42%, and 29% of OCCC tumours, respectively. The 3-year overall survival (OS) rate for patients with an activated PI3K/Akt signalling pathway was significantly higher than that for those with inactive pathway (91 vs 40%, hazard ratio 0.24 (95% confidence interval (CI) 0.10-0.56), P=0.0010). Similarly, the OS was significantly higher in patients with the activated RTK/Ras signalling pathway than in those with the inactive pathway (91 vs 53%, hazard ratio 0.35 (95% CI 0.13-0.94), P=0.0373). Multivariable analysis revealed that activation of the PI3K/Akt and RTK/Ras signalling pathways was an independent prognostic factor for patients with OCCC.

Conclusions: The PI3K/Akt and RTK/Ras signalling pathways may be potential prognostic biomarkers for OCCC patients. Furthermore, our whole-genome sequencing data highlight important pathways for molecular and biological characterisations and potential therapeutic targeting in OCCC.

MeSH terms

  • Adenocarcinoma, Clear Cell / genetics*
  • Adult
  • Aged
  • Aged, 80 and over
  • Biomarkers, Tumor / genetics
  • Carrier Proteins / genetics
  • DNA Helicases / genetics
  • DNA Mutational Analysis
  • DNA, Neoplasm / analysis*
  • DNA-Binding Proteins / genetics
  • Female
  • Genome, Human
  • Humans
  • Middle Aged
  • Molecular Targeted Therapy
  • Nerve Tissue Proteins / genetics
  • Nuclear Proteins / genetics*
  • Ovarian Neoplasms / genetics*
  • Phosphatidylinositol 3-Kinases / genetics*
  • Proto-Oncogene Proteins c-akt / genetics*
  • Receptor Protein-Tyrosine Kinases / genetics*
  • Repressor Proteins
  • Signal Transduction / genetics
  • Transcription Factors / genetics*
  • ras Proteins / genetics*

Substances

  • ARID1A protein, human
  • ARID1B protein, human
  • BCL11A protein, human
  • Biomarkers, Tumor
  • Carrier Proteins
  • DNA, Neoplasm
  • DNA-Binding Proteins
  • DPF1 protein, human
  • Nerve Tissue Proteins
  • Nuclear Proteins
  • Repressor Proteins
  • SMARCA1 protein, human
  • SMARCA2 protein, human
  • SMARCC1 protein, human
  • Transcription Factors
  • Receptor Protein-Tyrosine Kinases
  • Proto-Oncogene Proteins c-akt
  • SMARCA4 protein, human
  • DNA Helicases
  • ras Proteins