Comprehensive and Integrated Genomic Characterization of Adult Soft Tissue Sarcomas

Cell. 2017 Nov 2;171(4):950-965.e28. doi: 10.1016/j.cell.2017.10.014.

Abstract

Sarcomas are a broad family of mesenchymal malignancies exhibiting remarkable histologic diversity. We describe the multi-platform molecular landscape of 206 adult soft tissue sarcomas representing 6 major types. Along with novel insights into the biology of individual sarcoma types, we report three overarching findings: (1) unlike most epithelial malignancies, these sarcomas (excepting synovial sarcoma) are characterized predominantly by copy-number changes, with low mutational loads and only a few genes (TP53, ATRX, RB1) highly recurrently mutated across sarcoma types; (2) within sarcoma types, genomic and regulomic diversity of driver pathways defines molecular subtypes associated with patient outcome; and (3) the immune microenvironment, inferred from DNA methylation and mRNA profiles, associates with outcome and may inform clinical trials of immune checkpoint inhibitors. Overall, this large-scale analysis reveals previously unappreciated sarcoma-type-specific changes in copy number, methylation, RNA, and protein, providing insights into refining sarcoma therapy and relationships to other cancer types.

Keywords: DNA methylation; The Cancer Genome Atlas; dedifferentiated liposarcoma; genomics; immune infiltration; leiomyosarcoma; molecular subtype; myxofibrosarcoma; pleomorphism; undifferentiated pleomorphic sarcoma.

MeSH terms

  • Adult
  • Aged
  • Aged, 80 and over
  • Cluster Analysis
  • DNA Copy Number Variations
  • Epigenomics
  • Genome, Human
  • Genome-Wide Association Study
  • Humans
  • Middle Aged
  • Mutation
  • Sarcoma / diagnosis
  • Sarcoma / genetics*
  • Sarcoma / pathology
  • Young Adult