Adult maltase acid deficiency myopathy: treatment with long-term home mechanical ventilation

Biomed Pharmacother. 1988;42(5):343-9.

Abstract

We report a study of an adult with a maltase acid deficiency myopathy. A restrictive respiratory syndrome due to respiratory muscle weakness is associated with paralysis of other muscular groups. In 1982 the patient presented with an alveolar hypoventilation, and mechanical ventilation was required after acute respiratory failure. The patient has received nocturnal mechanical ventilation by tracheostomy at home for 5 years. His clinical status gradually improved in parallel to amelioration of his respiratory condition. Functional respiratory tests improved: initial hypoxia-hypercapnia disappeared, vital capacity increased. The possible mechanisms underlying the improvement are discussed. Increase in pulmonary compliance is an argument to explain the functional improvement observed. Ventilatory response to carbon dioxide was abnormal whereas the ventilatory response to exercise and maxima minute ventilation test were normal. Results are consistent with a respiratory control impairment. The role of mechanical ventilation is difficult to assess in the improvement we observed.

Publication types

  • Case Reports

MeSH terms

  • Adult
  • Home Care Services
  • Humans
  • Male
  • Neuromuscular Diseases / complications*
  • Neuromuscular Diseases / therapy
  • Respiration, Artificial*
  • Respiratory Function Tests
  • Respiratory Insufficiency / etiology
  • Respiratory Insufficiency / therapy*
  • Respiratory Paralysis / etiology
  • Respiratory Paralysis / therapy*
  • alpha-Glucosidases / deficiency*

Substances

  • alpha-Glucosidases