Discovery of ABBV-4083, a novel analog of Tylosin A that has potent anti-Wolbachia and anti-filarial activity

PLoS Negl Trop Dis. 2019 Feb 28;13(2):e0007159. doi: 10.1371/journal.pntd.0007159. eCollection 2019 Feb.

Abstract

There is a significant need for improved treatments for onchocerciasis and lymphatic filariasis, diseases caused by filarial worm infection. In particular, an agent able to selectively kill adult worms (macrofilaricide) would be expected to substantially augment the benefits of mass drug administration (MDA) with current microfilaricides, and to provide a solution to treatment of onchocerciasis / loiasis co-infection, where MDA is restricted. We have identified a novel macrofilaricidal agent, Tylosin A (TylA), which acts by targeting the worm-symbiont Wolbachia bacterium. Chemical modification of TylA leads to improvements in anti-Wolbachia activity and oral pharmacokinetic properties; an optimized analog (ABBV-4083) has been selected for clinical evaluation.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Anti-Bacterial Agents / pharmacokinetics
  • Anti-Bacterial Agents / pharmacology*
  • Drug Discovery*
  • Elephantiasis, Filarial / drug therapy
  • Female
  • Filaricides / pharmacokinetics
  • Filaricides / pharmacology*
  • Filarioidea / drug effects
  • Filarioidea / microbiology
  • Gerbillinae
  • Mice
  • Mice, Inbred BALB C
  • Onchocerciasis / drug therapy
  • Symbiosis / drug effects
  • Tylosin / analogs & derivatives*
  • Tylosin / pharmacology*
  • Wolbachia / drug effects*

Substances

  • Anti-Bacterial Agents
  • Filaricides
  • Tylosin