Bone marrow transplantation for Hurler syndrome: assessment of metabolic correction

Birth Defects Orig Artic Ser. 1986;22(1):7-24.
No abstract available

MeSH terms

  • Bone Marrow Transplantation*
  • Child, Preschool
  • Heterozygote
  • Homozygote
  • Humans
  • Iduronidase / blood
  • Leukocytes / enzymology
  • Methods
  • Mucopolysaccharidosis I / enzymology
  • Mucopolysaccharidosis I / genetics
  • Mucopolysaccharidosis I / therapy*

Substances

  • Iduronidase