[Which follow-up for innovative treatments?]

Med Sci (Paris). 2019 Mar:35 Hors série n° 1:54-56. doi: 10.1051/medsci/2019053. Epub 2019 Apr 3.
[Article in French]
No abstract available

MeSH terms

  • Adverse Drug Reaction Reporting Systems
  • Drug Monitoring / methods
  • Drug Monitoring / standards
  • Drug-Related Side Effects and Adverse Reactions / diagnosis
  • Drug-Related Side Effects and Adverse Reactions / therapy
  • Follow-Up Studies
  • Glycogen Storage Disease Type II / drug therapy
  • Glycogen Storage Disease Type II / physiopathology
  • Humans
  • Locomotion / drug effects
  • Monitoring, Physiologic / methods*
  • Monitoring, Physiologic / standards
  • Neuromuscular Diseases / drug therapy
  • Neuromuscular Diseases / physiopathology
  • Registries
  • Research Design / standards
  • Respiration
  • Respiratory Function Tests
  • Therapies, Investigational / methods*
  • Therapies, Investigational / standards
  • Treatment Outcome
  • alpha-Glucosidases / therapeutic use

Substances

  • GAA protein, human
  • alpha-Glucosidases