Colony-stimulating factor 1 and its receptor are new potential therapeutic targets for allergic asthma

Allergy. 2020 Feb;75(2):357-369. doi: 10.1111/all.14011. Epub 2019 Oct 11.

Abstract

Background: A new approach targeting aeroallergen sensing in the early events of mucosal immunity could have greater benefit. The CSF1-CSF1R pathway has a critical role in trafficking allergens to regional lymph nodes through activating dendritic cells. Intervention in this pathway could prevent allergen sensitization and subsequent Th2 allergic inflammation.

Objective: To examine the therapeutic effectiveness of CSF1 and CSF1R inhibition for blocking the dendritic cell function of sensing aeroallergens.

Methods: We adopted a model of chronic asthma induced by a panel of three naturally occurring allergens and novel delivery system of CSF1R inhibitor encapsulated nanoprobe.

Results: Selective depletion of CSF1 in airway epithelial cells abolished the production of allergen-reactive IgE, resulting in prevention of new asthma development as well as reversal of established allergic lung inflammation. CDPL-GW nanoprobe containing GW2580, a selective CSF1R inhibitor, showed favorable pharmacokinetics for inhalational treatment and intranasal insufflation delivery of CDPL-GW nanoprobe ameliorated asthma pathologies including allergen-specific serum IgE production, allergic lung and airway inflammation and airway hyper-responsiveness (AHR) with minimal pulmonary adverse reaction.

Conclusion: The inhibition of the CSF1-CSF1R signaling pathway effectively suppresses sensitization to aeroallergens and consequent allergic lung inflammation in a murine model of chronic asthma. CSF1R inhibition is a promising new target for the treatment of allergic asthma.

Keywords: CSF1; CSF1R; airway epithelial cells; airway remodeling; asthma therapy; chronic inflammation; dendritic cells.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Allergens / immunology
  • Allergens / pharmacology
  • Animals
  • Anisoles / administration & dosage*
  • Anisoles / pharmacology*
  • Asthma / chemically induced
  • Asthma / drug therapy*
  • Disease Models, Animal
  • Drug Delivery Systems / methods*
  • Female
  • Immunoglobulin E / biosynthesis
  • Macrophage Colony-Stimulating Factor / antagonists & inhibitors*
  • Macrophage Colony-Stimulating Factor / genetics
  • Macrophage Colony-Stimulating Factor / metabolism*
  • Male
  • Mice
  • Mice, Inbred C57BL
  • Mice, Transgenic
  • Nanostructures / administration & dosage
  • Pyrimidines / administration & dosage*
  • Pyrimidines / pharmacology*
  • Quaternary Ammonium Compounds / administration & dosage
  • Receptors, Granulocyte-Macrophage Colony-Stimulating Factor / genetics
  • Receptors, Granulocyte-Macrophage Colony-Stimulating Factor / metabolism*
  • Signal Transduction / drug effects
  • Signal Transduction / genetics
  • Signal Transduction / immunology
  • Sulfonic Acids / administration & dosage
  • Treatment Outcome

Substances

  • 5-(3-methoxy-4-((4-methoxybenzyl)oxy)benzyl)pyrimidine-2,4-diamine
  • Allergens
  • Anisoles
  • CSF1 protein, mouse
  • Csf1r protein, mouse
  • Pyrimidines
  • Quaternary Ammonium Compounds
  • Receptors, Granulocyte-Macrophage Colony-Stimulating Factor
  • Sulfonic Acids
  • ZW800-1 compound
  • Immunoglobulin E
  • Macrophage Colony-Stimulating Factor