Absence of Collagen Flowers on Electron Microscopy and Identification of (Likely) Pathogenic COL5A1 Variants in Two Patients

Genes (Basel). 2019 Sep 27;10(10):762. doi: 10.3390/genes10100762.

Abstract

Two probands are reported with pathogenic and likely pathogenic COL5A1 variants (frameshift and splice site) in whom no collagen flowers have been identified with transmission electron microscopy (TEM). One proband fulfils the clinical criteria for classical Ehlers-Danlos syndrome (cEDS) while the other does not and presents with a vascular complication. This case report highlights the significant intrafamilial variability within the cEDS phenotype and demonstrates that patients with pathogenic COL5A1 variants can have an absence of collagen flowers on TEM skin biopsy analysis. This has not been previously reported in the literature and is important when evaluating the significance of a TEM result in patients with clinically suspected cEDS and underscores the relevance of molecular analysis.

Keywords: COL5A1; classical Ehlers-Danlos Syndrome; collagen flowers; electron microscopy.

Publication types

  • Case Reports

MeSH terms

  • Adult
  • Codon, Nonsense
  • Collagen Type V / genetics*
  • Dermis / ultrastructure*
  • Ehlers-Danlos Syndrome / genetics*
  • Ehlers-Danlos Syndrome / pathology
  • Female
  • Frameshift Mutation
  • Humans
  • Middle Aged
  • Pedigree

Substances

  • COL5A1 protein, human
  • Codon, Nonsense
  • Collagen Type V