Targeted deep sequencing of cell-free DNA in serous body cavity fluids with malignant, suspicious, and benign cytology

Cancer Cytopathol. 2020 Jan;128(1):43-56. doi: 10.1002/cncy.22205. Epub 2019 Nov 21.

Abstract

Background: Liquid biopsy using cell-free DNA (cfDNA) presents new opportunities for solid tumor genotyping. While studies have demonstrated the utility of cfDNA from plasma, cfDNA from other body fluids remains underexplored.

Methods: We evaluated the molecular features and clinicopathologic correlates of cfDNA from serous body cavity fluids by performing hybrid capture-based next-generation sequencing (NGS) on cfDNA isolated from residual effusion supernatants. Twenty-one serous effusions from pleural (n = 15), peritoneal (n = 5), and pericardial (n = 1) cavity were analyzed.

Results: The supernatants provided a median cfDNA concentration of 10.3 ng/µL. Notably, all effusions were sequenced successfully to a median depth >1000×, revealing a broad range of genetic alterations including single nucleotide variants, small insertions and deletions, amplifications, and fusions. Specifically, pathogenic alterations were identified in all malignant fluids (13/13), all fluids suspicious for malignancy (2/2), and 1 benign fluid (1/6) from a patient with metastatic cancer. To validate our findings, we examined matching results from 11 patients who underwent additional testing using formalin-fixed, paraffin-embedded (FFPE) specimens. In 8 patients, the paired results between FFPE and supernatant testing were concordant, whereas in the remaining 3 patients, supernatant analysis identified additional variants likely associated with resistance to targeted therapies. Additional comparison between FFPE and supernatant testing showed no difference in DNA concentration (P = .5), depth of coverage (P = .6), or allele frequency of pathogenic mutations (P = .7).

Conclusion: cfDNA isolated from serous body cavity fluids represents a promising source of genomic input for targeted NGS.

Keywords: cell-free DNA; effusion cytology; molecular diagnostics; molecular pathology; non-gynecologic cytology.

MeSH terms

  • Adult
  • Aged
  • Aged, 80 and over
  • Biomarkers, Tumor / analysis*
  • Biomarkers, Tumor / genetics
  • Body Fluids / chemistry*
  • Circulating Tumor DNA / analysis*
  • Circulating Tumor DNA / genetics
  • Female
  • Genotyping Techniques / methods*
  • High-Throughput Nucleotide Sequencing
  • Humans
  • Liquid Biopsy / methods
  • Male
  • Middle Aged
  • Neoplasms / diagnosis*
  • Neoplasms / genetics
  • Neoplasms / pathology

Substances

  • Biomarkers, Tumor
  • Circulating Tumor DNA