Protein Footprinting and X-ray Crystallography Reveal the Interaction of PD-L1 and a Macrocyclic Peptide

Biochemistry. 2020 Feb 4;59(4):541-551. doi: 10.1021/acs.biochem.9b00822. Epub 2019 Dec 31.

Abstract

Blocking interactions between PD-1 and PD-L1 opens a new era of cancer treatment involving immunity modulation. Although most immunotherapies use monoclonal antibodies, small-molecule inhibitors offer advantages. To facilitate development of small-molecule therapeutics, we implemented a rapid approach to characterize the binding interfaces of small-molecule inhibitors with PD-L1. We determined its interaction with a synthetic macrocyclic peptide by using two mass spectrometry-based approaches, hydrogen-deuterium exchange and fast photochemical oxidation of proteins (FPOP), and corroborated the findings with our X-ray structure of the PD-L1/macrocycle complex. Although all three approaches show that the macrocycle binds directly to PD-L1 over the regions of residues 46-87 and 114-125, the two protein footprinting approaches show additional binding at the N-terminus of PD-L1, and FPOP reveals some critical binding residues. The outcomes not only show the binding regions but also demonstrate the utility of MS-based footprinting in probing protein/ligand inhibitory interactions in cancer immunotherapy.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Antibodies, Monoclonal / chemistry
  • B7-H1 Antigen / antagonists & inhibitors*
  • B7-H1 Antigen / chemistry*
  • B7-H1 Antigen / metabolism
  • Crystallography, X-Ray / methods
  • Humans
  • Immunotherapy
  • Ligands
  • Macrocyclic Compounds / chemistry
  • Macrocyclic Compounds / pharmacology
  • Mass Spectrometry
  • Models, Molecular
  • Oxidation-Reduction
  • Peptides / chemistry
  • Programmed Cell Death 1 Receptor / immunology
  • Programmed Cell Death 1 Receptor / metabolism
  • Protein Footprinting / methods
  • Small Molecule Libraries / pharmacology

Substances

  • Antibodies, Monoclonal
  • B7-H1 Antigen
  • CD274 protein, human
  • Ligands
  • Macrocyclic Compounds
  • Peptides
  • Programmed Cell Death 1 Receptor
  • Small Molecule Libraries