Mutations in COPA lead to abnormal trafficking of STING to the Golgi and interferon signaling

J Exp Med. 2020 Nov 2;217(11):e20200600. doi: 10.1084/jem.20200600.

Abstract

Heterozygous missense mutations in coatomer protein subunit α, COPA, cause a syndrome overlapping clinically with type I IFN-mediated disease due to gain-of-function in STING, a key adaptor of IFN signaling. Recently, increased levels of IFN-stimulated genes (ISGs) were described in COPA syndrome. However, the link between COPA mutations and IFN signaling is unknown. We observed elevated levels of ISGs and IFN-α in blood of symptomatic COPA patients. In vitro, both overexpression of mutant COPA and silencing of COPA induced STING-dependent IFN signaling. We detected an interaction between COPA and STING, and mutant COPA was associated with an accumulation of ER-resident STING at the Golgi. Given the known role of the coatomer protein complex I, we speculate that loss of COPA function leads to enhanced type I IFN signaling due to a failure of Golgi-to-ER STING retrieval. These data highlight the importance of the ER-Golgi axis in the control of autoinflammation and inform therapeutic strategies in COPA syndrome.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adolescent
  • Adult
  • Child
  • Coatomer Protein / genetics*
  • Coatomer Protein / metabolism*
  • Endoplasmic Reticulum / metabolism
  • Female
  • Gene Knockout Techniques
  • Golgi Apparatus / metabolism*
  • HEK293 Cells
  • Humans
  • Interferon Type I / metabolism*
  • Male
  • Membrane Proteins / genetics
  • Membrane Proteins / metabolism*
  • Middle Aged
  • Mutation, Missense*
  • Protein Transport / genetics
  • Signal Transduction / genetics*
  • THP-1 Cells
  • Transfection
  • Young Adult

Substances

  • Coatomer Protein
  • Interferon Type I
  • Membrane Proteins
  • STING1 protein, human