Ryanodine Receptors: A Potential Treatment Target in Various Neurodegenerative Disease

Cell Mol Neurobiol. 2021 Nov;41(8):1613-1624. doi: 10.1007/s10571-020-00936-w. Epub 2020 Aug 24.

Abstract

Progressive neuronal demise is a key contributor to the key pathogenic event implicated in many different neurodegenerative disorders (NDDs). There are several therapeutic strategies available; however, none of them are particularly effective. Targeted neuroprotective therapy is one such therapy, which seems a compelling option, yet remains challenging due to the internal heterogeneity of the mechanisms underlying various NDDs. An alternative method to treat NDDs is to exploit common modalities involving molecularly distinct subtypes and thus develop specialized drugs with broad-spectrum characteristics. There is mounting evidence which supports for the theory that dysfunctional ryanodine receptors (RyRs) disrupt intracellular Ca2+ homeostasis, contributing to NDDs significantly. This review aims to provide direct and indirect evidence on the intersection of NDDs and RyRs malfunction, and to shed light on novel strategies to treat RyRs-mediated disease, modifying pharmacological therapies such as the potential therapeutic role of dantrolene, a RyRs antagonist.

Keywords: Apoptosis; Autophagy; Calcium; Dantrolene; Endoplasmic reticulum; Mitochondria; Neurodegenerative disorders; Ryanodine receptor.

Publication types

  • Review

MeSH terms

  • Animals
  • Brain / drug effects
  • Brain / metabolism
  • Calcium Channel Blockers / administration & dosage*
  • Calcium Signaling / drug effects
  • Calcium Signaling / physiology*
  • Dantrolene / administration & dosage*
  • Humans
  • Neurodegenerative Diseases / drug therapy
  • Neurodegenerative Diseases / metabolism*
  • Neurons / drug effects
  • Neurons / metabolism
  • Ryanodine Receptor Calcium Release Channel / metabolism*

Substances

  • Calcium Channel Blockers
  • Ryanodine Receptor Calcium Release Channel
  • Dantrolene