Lower risk of severe checkpoint inhibitor toxicity in more advanced disease

ESMO Open. 2020 Nov;5(6):e000945. doi: 10.1136/esmoopen-2020-000945.

Abstract

Background: Immune checkpoint inhibitor (ICI) can cause severe and sometimes fatal immune-related adverse events (irAEs). Since these irAEs mimick immunological disease, a female predominance has been speculated on. Nevertheless, no demographic or tumour-related factors associated with an increased risk of irAEs have been identified until now.

Methods: Risk ratios of severe (grade ≥3) irAEs for age, sex, WHO performance status, number of comorbidities, stage of disease, number of metastases and serum lactate dehydrogenases (LDH) were estimated using data from anti-PD1-treated patients with advanced melanoma in the prospective nationwide Dutch Melanoma Treatment Registry.

Results: 111 (11%) out of 819 anti-programmed cell death 1 treated patients experienced severe irAEs. Patients with non-lung visceral metastases (stage IV M1c or higher) less often experienced severe irAEs (11%) compared with patients with only lung and/or lymph node/soft tissue involvement (stage IV M1b or lower; 19%; adjusted risk ratio (RRadj) 0.63; 95% CI 0.41 to 0.94). Patients with LDH of more than two times upper limit of normal had a non-significantly lower risk of developing severe irAEs than those with normal LDH (RRadj 0.65; 95% CI 0.20 to 2.13). None of the other variables were associated with severe irAEs.

Conclusion: In patients with melanoma, more advanced disease is associated with a lower rate of severe irAEs. No association with sex was found.

Keywords: DMTR; anti-PD1; checkpoint inhibition; immune-related adverse event (irAE); melanoma.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Antineoplastic Agents, Immunological* / therapeutic use
  • Female
  • Humans
  • Melanoma* / drug therapy
  • Melanoma* / epidemiology
  • Programmed Cell Death 1 Receptor
  • Prospective Studies
  • Retrospective Studies

Substances

  • Antineoplastic Agents, Immunological
  • Programmed Cell Death 1 Receptor