Infantile fibrosarcoma with TPM3-NTRK1 fusion in a boy with Bloom syndrome

Fam Cancer. 2022 Jan;21(1):85-90. doi: 10.1007/s10689-020-00221-1. Epub 2020 Nov 21.

Abstract

Bloom syndrome (BS) is a genomic and chromosomal instability disorder with prodigious cancer predisposition caused by pathogenic variants in BLM. We report the clinical and genetic details of a boy who first presented with infantile fibrosarcoma (IFS) at the age of 6 months and subsequently was diagnosed with BS at the age of 9 years. Molecular analysis identified the pathogenic germline BLM sequence variants (c.1642C>T and c.2207_2212delinsTAGATTC). This is the first report of IFS related to BS, for which we show that both BLM alleles are maintained in the tumor and demonstrate a TPM3-NTKR1 fusion transcript in the IFS. Our communication emphasizes the importance of long-term follow up after treatment for pediatric neoplastic conditions, as clues to important genetic entities might manifest later, and the identification of a heritable tumor predisposition often leads to changes in patient surveillance and management.

Keywords: Bloom syndrome; Cancer predisposition; Infantile fibrosarcoma; TPM3-NTKR1 fusion.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Alleles
  • Bloom Syndrome* / genetics
  • Child
  • Fibrosarcoma* / genetics
  • Genetic Predisposition to Disease
  • Genotype
  • Humans
  • Infant
  • Male
  • RecQ Helicases / genetics
  • Tropomyosin / genetics
  • Tropomyosin / therapeutic use

Substances

  • TPM3 protein, human
  • Tropomyosin
  • RecQ Helicases