Outcome Squares Integrating Efficacy and Safety, as Applied to Functioning Pituitary Adenoma Surgery

J Clin Endocrinol Metab. 2021 Aug 18;106(9):e3300-e3311. doi: 10.1210/clinem/dgab138.

Abstract

Context: Transsphenoidal surgery is standard care in the treatment of hormone-secreting pituitary adenomas. Current clinician-reported surgical outcome measures are one-dimensional, typically focusing primarily on complete or partial resection, and secondarily on complication rates. However, outcomes are best reflected by the delicate balance of efficacy and complications at patient level.

Objective: This study proposes a novel way to classify and report outcomes, integrating efficacy and safety at the patient level.

Methods: Retrospective chart review of all pure endoscopic transsphenoidal surgical procedures for acromegaly, Cushing's disease, and prolactinoma between 2010 and 2018 in a single tertiary referral center. We present our results in a classic (remission and complications separate) and in a novel outcome square integrating both outcomes, focusing on intended and adverse effects (long-term complications). This resulted in 4 outcome groups, ranging from good to poor. We use this approach to present these outcomes for several subgroups.

Results: A total of 198 surgical procedures were included (44 reoperations). Remission was achieved in 127 operations (64%). Good outcome was observed after 121 (61%), and poor outcome after 6 (3%) operations. When intended effect of surgery was applied (instead of remission), good outcome as intended was achieved after 148 of 198 surgeries (75%) and poor outcome after 4 (2%).

Conclusion: Quality of a surgical intervention can be presented in 4 simple categories, integrating both efficacy and safety with flexibility to adapt to the individualized situation at patient, disease, and surgical strategy and to the outcome of interest.

Keywords: Pituitary adenoma; outcomes; patient counselling; transsphenoidal surgery.

MeSH terms

  • Acromegaly / surgery
  • Adenoma / surgery*
  • Adult
  • Aged
  • Endocrine Surgical Procedures / adverse effects
  • Endocrine Surgical Procedures / classification*
  • Endocrine Surgical Procedures / statistics & numerical data
  • Female
  • Humans
  • Magnetic Resonance Imaging
  • Male
  • Middle Aged
  • Neoplasm Recurrence, Local
  • Neurosurgical Procedures / adverse effects
  • Neurosurgical Procedures / classification*
  • Neurosurgical Procedures / statistics & numerical data
  • Pituitary ACTH Hypersecretion / surgery
  • Pituitary Neoplasms / surgery*
  • Postoperative Complications / epidemiology
  • Prolactinoma / surgery
  • Reoperation / statistics & numerical data
  • Retrospective Studies
  • Sphenoid Bone / surgery
  • Treatment Outcome