Stereo- and regiodefined DNA-encoded chemical libraries enable efficient tumour-targeting applications

Nat Chem. 2021 Jun;13(6):540-548. doi: 10.1038/s41557-021-00660-y. Epub 2021 Apr 8.

Abstract

The encoding of chemical compounds with amplifiable DNA tags facilitates the discovery of small-molecule ligands for proteins. To investigate the impact of stereo- and regiochemistry on ligand discovery, we synthesized a DNA-encoded library of 670,752 derivatives based on 2-azido-3-iodophenylpropionic acids. The library was selected against multiple proteins and yielded specific ligands. The selection fingerprints obtained for a set of protein targets of pharmaceutical relevance clearly showed the preferential enrichment of ortho-, meta- or para-regioisomers, which was experimentally verified by affinity measurements in the absence of DNA. The discovered ligands included novel selective enzyme inhibitors and binders to tumour-associated antigens, which enabled conditional chimeric antigen receptor T-cell activation and tumour targeting.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Cell Line, Tumor
  • DNA / chemistry
  • Drug Delivery Systems*
  • Drug Discovery
  • Fluorescence
  • Gene Library
  • Humans
  • Immunoglobulin Variable Region / chemistry
  • Immunoglobulin Variable Region / pharmacology*
  • Mice
  • Microscopy, Fluorescence
  • Neoplasms
  • Neoplasms, Experimental
  • Receptors, Chimeric Antigen / metabolism*
  • T-Lymphocytes / drug effects*
  • T-Lymphocytes / metabolism*

Substances

  • Immunoglobulin Variable Region
  • Receptors, Chimeric Antigen
  • DNA