Noninvasive Detection of Hepatocellular Carcinoma with Circulating Tumor DNA Features and α-Fetoprotein

J Mol Diagn. 2021 Sep;23(9):1174-1184. doi: 10.1016/j.jmoldx.2021.06.003. Epub 2021 Jun 26.

Abstract

Liver cancer is the fifth-most common cancer worldwide, with the third-highest rate of cancer-related mortality. Hepatocellular carcinoma (HCC) is the leading pathologic subtype, contributing 85% to 90% of cases of primary liver cancer. Most HCC patients are diagnosed at an advanced stage at which treatment is not curative. This study assessed the performance of a newly developed blood-based assay that utilizes genomic features and protein markers for the early detection of HCC. Two cancer-associated hallmarks, copy-number aberrations (CNA) and fragment size (FS), were characterized by shallow whole-genome sequencing of cell-free DNA and utilized to differentiate cancer patients from healthy subjects. As a clinically implemented biomarker of HCC, plasma α-fetoprotein (AFP) was also used with the genomic surrogates to optimize the detection of HCCs. The sensitivity of AFP ≥20.0 μg/L in detecting HCC was 57.9%. The combined genomic classifier CNA + FS via cell-free DNA shallow whole-genome sequencing identified nearly half of AFP-negative HCC patients (43.8%). By integrating CNA, FS as well as AFP (HCCseek), 75.0% sensitivity was achieved at 98.0% specificity, resulting in 92.6% accuracy, with 58.6% sensitivity in stage I HCC. The quantitative output of HCCseek was correlated with the severity of the disease (tumor size, stage, and recurrence-free survival). In summary, this study describes an efficient, noninvasive, and cost-effective method to detect HCC.

Keywords: AFP; CNA; HCC; early detection; fragment size.

MeSH terms

  • Adult
  • Aged
  • Biomarkers, Tumor / blood
  • Carcinoma, Hepatocellular / blood*
  • Carcinoma, Hepatocellular / diagnosis*
  • Case-Control Studies
  • Circulating Tumor DNA / blood*
  • Circulating Tumor DNA / genetics
  • Circulating Tumor DNA / isolation & purification
  • Cost-Benefit Analysis
  • DNA Copy Number Variations
  • Data Accuracy
  • Early Detection of Cancer / economics
  • Early Detection of Cancer / methods*
  • Female
  • Humans
  • Liver Neoplasms / blood*
  • Liver Neoplasms / diagnosis*
  • Male
  • Middle Aged
  • Sensitivity and Specificity
  • alpha-Fetoproteins / analysis*

Substances

  • AFP protein, human
  • Biomarkers, Tumor
  • Circulating Tumor DNA
  • alpha-Fetoproteins