A lysosome-targeted DNA nanodevice selectively targets macrophages to attenuate tumours

Nat Nanotechnol. 2021 Dec;16(12):1394-1402. doi: 10.1038/s41565-021-00988-z. Epub 2021 Nov 11.

Abstract

Activating CD8+ T cells by antigen cross-presentation is remarkably effective at eliminating tumours. Although this function is traditionally attributed to dendritic cells, tumour-associated macrophages (TAMs) can also cross-present antigens. TAMs are the most abundant tumour-infiltrating leukocyte. Yet, TAMs have not been leveraged to activate CD8+ T cells because mechanisms that modulate their ability to cross-present antigens are incompletely understood. Here we show that TAMs harbour hyperactive cysteine protease activity in their lysosomes, which impedes antigen cross-presentation, thereby preventing CD8+ T cell activation. We developed a DNA nanodevice (E64-DNA) that targets the lysosomes of TAMs in mice. E64-DNA inhibits the population of cysteine proteases that is present specifically inside the lysosomes of TAMs, improves their ability to cross-present antigens and attenuates tumour growth via CD8+ T cells. When combined with cyclophosphamide, E64-DNA showed sustained tumour regression in a triple-negative-breast-cancer model. Our studies demonstrate that DNA nanodevices can be targeted with organelle-level precision to reprogram macrophages and achieve immunomodulation in vivo.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Antigens / metabolism
  • Basic Helix-Loop-Helix Leucine Zipper Transcription Factors / deficiency
  • Basic Helix-Loop-Helix Leucine Zipper Transcription Factors / metabolism
  • CD8-Positive T-Lymphocytes / immunology
  • Cell Proliferation
  • Combined Modality Therapy
  • Cross-Priming / immunology
  • Cyclophosphamide
  • DNA / chemistry*
  • Female
  • Humans
  • Immunity
  • Lysosomes / metabolism*
  • Mice
  • Mice, Inbred C57BL
  • Nanoparticles / chemistry*
  • Neoplasms / immunology
  • Neoplasms / pathology*
  • Proteomics
  • Tumor-Associated Macrophages / metabolism*

Substances

  • Antigens
  • Basic Helix-Loop-Helix Leucine Zipper Transcription Factors
  • Tcfeb protein, mouse
  • Cyclophosphamide
  • DNA