A solid start for gene therapy in Tay-Sachs disease
Nat Med
.
2022 Feb;28(2):236-237.
doi: 10.1038/s41591-022-01687-5.
Authors
Timothy W Yu
1
2
3
4
,
Olaf Bodamer
5
6
7
Affiliations
1
Division of Genetics and Genomics, Boston Children's Hospital, Boston, MA, USA. timothy.yu@childrens.harvard.edu.
2
Broad Institute of MIT and Harvard, Cambridge, MA, USA. timothy.yu@childrens.harvard.edu.
3
Harvard Medical School, Boston, MA, USA. timothy.yu@childrens.harvard.edu.
4
Department of Neurology, Boston Children's Hospital, Boston, MA, USA. timothy.yu@childrens.harvard.edu.
5
Division of Genetics and Genomics, Boston Children's Hospital, Boston, MA, USA.
6
Broad Institute of MIT and Harvard, Cambridge, MA, USA.
7
Harvard Medical School, Boston, MA, USA.
PMID:
35145310
DOI:
10.1038/s41591-022-01687-5
No abstract available
Publication types
Comment
MeSH terms
Genetic Therapy
Humans
Tay-Sachs Disease* / genetics
Tay-Sachs Disease* / therapy