What's next in gene therapy for Crigler-Najjar syndrome?

Expert Opin Biol Ther. 2023 Feb;23(2):119-121. doi: 10.1080/14712598.2022.2160237. Epub 2022 Dec 29.

Authors

Sem J Aronson¹, Giuseppe Ronzitti^{2

3}, Piter J Bosma¹

Affiliations

¹ Amsterdam UMC, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, BK Amsterdam, The Netherlands.
² Genethon, Evry, France.
³ Integrare Research Unit UMR_S951, Université Paris-Saclay, Univ Evry, Inserm, Genethon, Evry, France.

PMID: 36579791
DOI: 10.1080/14712598.2022.2160237

No abstract available

Publication types

Editorial

MeSH terms

Crigler-Najjar Syndrome* / genetics
Crigler-Najjar Syndrome* / therapy
Genetic Therapy / adverse effects
Humans