Targeting RNA G-quadruplex with repurposed drugs blocks SARS-CoV-2 entry

PLoS Pathog. 2023 Jan 26;19(1):e1011131. doi: 10.1371/journal.ppat.1011131. eCollection 2023 Jan.

Abstract

The rapid emergence of SARS-CoV-2 variants of concern, the complexity of infection, and the functional redundancy of host factors, underscore an urgent need for broad-spectrum antivirals against the continuous COVID-19 pandemic, with drug repurposing as a viable therapeutic strategy. Here we report the potential of RNA G-quadruplex (RG4)-targeting therapeutic strategy for SARS-CoV-2 entry. Combining bioinformatics, biochemical and biophysical approaches, we characterize the existence of RG4s in several SARS-CoV-2 host factors. In silico screening followed by experimental validation identify Topotecan (TPT) and Berbamine (BBM), two clinical approved drugs, as RG4-stabilizing agents with repurposing potential for COVID-19. Both TPT and BBM can reduce the protein level of RG4-containing host factors, including ACE2, AXL, FURIN, and TMPRSS2. Intriguingly, TPT and BBM block SARS-CoV-2 pseudovirus entry into target cells in vitro and murine tissues in vivo. These findings emphasize the significance of RG4 in SARS-CoV-2 pathogenesis and provide a potential broad-spectrum antiviral strategy for COVID-19 prevention and treatment.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Antiviral Agents / metabolism
  • COVID-19*
  • Humans
  • Mice
  • Pandemics
  • RNA
  • SARS-CoV-2* / metabolism
  • Spike Glycoprotein, Coronavirus
  • Virus Internalization

Substances

  • RNA
  • Antiviral Agents
  • Spike Glycoprotein, Coronavirus
  • spike protein, SARS-CoV-2

Supplementary concepts

  • SARS-CoV-2 variants

Grants and funding

This work was supported by National Natural Science Foundation of China (92157205 and 81970561 to X.F.; 82172986 to Y.T.; 82173182 to D.L.; 82000547 to G.L.); the National Key R&D Program of China (2018YFC2000305), the 1.3.5 Project for Disciplines of Excellence, West China Hospital, Sichuan University (ZYJC18049 to X.F.; ZYYC20007); National Clinical Research Center for Geriatrics, West China Hospital, Sichuan University (Z20201003); the Fellowship of China Postdoctoral Science Foundation (2020TQ0215 and 2021M690112 to G.L.); and Sichuan University Postdoctoral Interdisciplinary Innovation Fund to G.L. The funders had no role in study design, data collection and analysis, decision to publish, or preparation of the manuscript.