Inborn Error of STAT2-Dependent IFN-I Immunity in a Patient Presented with Hemophagocytic Lymphohistiocytosis and Multisystem Inflammatory Syndrome in Children

J Clin Immunol. 2023 Aug;43(6):1278-1288. doi: 10.1007/s10875-023-01488-6. Epub 2023 Apr 19.

Abstract

Human inborn errors of immunity (IEI) affecting the type I interferon (IFN-I) induction pathway have been associated with predisposition to severe viral infections. Hemophagocytic lymphohistiocytosis (HLH) is a life-threatening systemic hyperinflammatory syndrome that has been increasingly associated with inborn errors of IFN-I-mediated innate immunity. Here is reported a novel case of complete deficiency of STAT2 in a 3-year-old child that presented with typical features of HLH after mumps, measles, and rubella vaccination at the age of 12 months. Due to the life-threatening risk of viral infection, she received SARS-CoV-2 mRNA vaccination. Unfortunately, she developed multisystem inflammatory syndrome in children (MIS-C) after SARS-CoV-2 infection, 4 months after the last dose. Functional studies showed an impaired IFN-I-induced response and a defective IFNα expression at later stages of STAT2 pathway induction. These results suggest a possible more complex mechanism for hyperinflammatory reactions in this type of patients involving a possible defect in the IFN-I production. Understanding the cellular and molecular links between IFN-I-induced signaling and hyperinflammatory syndromes can be critical for the diagnosis and tailored management of these patients with predisposition to severe viral infection.

Keywords: IFNα; Innate immunity; Interferons; SARS-CoV-2; STAT2 deficiency; Viral susceptibility.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Antibodies
  • COVID-19*
  • Child, Preschool
  • Female
  • Humans
  • Infant
  • Interferon Type I* / metabolism
  • Lymphohistiocytosis, Hemophagocytic* / diagnosis
  • SARS-CoV-2
  • STAT2 Transcription Factor / genetics

Substances

  • Interferon Type I
  • Antibodies
  • STAT2 protein, human
  • STAT2 Transcription Factor

Supplementary concepts

  • pediatric multisystem inflammatory disease, COVID-19 related