TRIM11 protects against tauopathies and is down-regulated in Alzheimer's disease

Science. 2023 Jul 28;381(6656):eadd6696. doi: 10.1126/science.add6696. Epub 2023 Jul 28.

Abstract

Aggregation of tau into filamentous inclusions underlies Alzheimer's disease (AD) and numerous other neurodegenerative tauopathies. The pathogenesis of tauopathies remains unclear, which impedes the development of disease-modifying treatments. Here, by systematically analyzing human tripartite motif (TRIM) proteins, we identified a few TRIMs that could potently inhibit tau aggregation. Among them, TRIM11 was markedly down-regulated in AD brains. TRIM11 promoted the proteasomal degradation of mutant tau as well as superfluous normal tau. It also enhanced tau solubility by acting as both a molecular chaperone to prevent tau misfolding and a disaggregase to dissolve preformed tau fibrils. TRIM11 maintained the connectivity and viability of neurons. Intracranial delivery of TRIM11 through adeno-associated viruses ameliorated pathology, neuroinflammation, and cognitive impairments in multiple animal models of tauopathies. These results suggest that TRIM11 down-regulation contributes to the pathogenesis of tauopathies and that restoring TRIM11 expression may represent an effective therapeutic strategy.

MeSH terms

  • Alzheimer Disease / genetics
  • Alzheimer Disease / metabolism
  • Animals
  • Brain / metabolism
  • Humans
  • Neurons / metabolism
  • Protein Aggregation, Pathological*
  • Tauopathies* / genetics
  • Tauopathies* / metabolism
  • Tripartite Motif Proteins / genetics
  • Tripartite Motif Proteins / metabolism
  • Ubiquitin-Protein Ligases / genetics
  • Ubiquitin-Protein Ligases / metabolism
  • tau Proteins / genetics
  • tau Proteins / metabolism

Substances

  • tau Proteins
  • TRIM11 protein, human
  • Tripartite Motif Proteins
  • Ubiquitin-Protein Ligases