A circulating cell-free DNA methylation signature for the detection of hepatocellular carcinoma

Mol Cancer. 2023 Oct 6;22(1):164. doi: 10.1186/s12943-023-01872-1.

Abstract

To address the shortcomings of current hepatocellular carcinoma (HCC) surveillance tests, we set out to find HCC-specific methylation markers and develop a highly sensitive polymerase chain reaction (PCR)-based method to detect them in circulating cell-free DNA (cfDNA). The analysis of large methylome data revealed that Ring Finger Protein 135 (RNF135) and Lactate Dehydrogenase B (LDHB) are universally applicable HCC methylation markers with no discernible methylation level detected in any other tissue types. These markers were used to develop Methylation Sensitive High-Resolution Analysis (MS-HRM), and their diagnostic accuracy was tested using cfDNA from healthy, at-risk, and HCC patients. The combined MS-HRM RNF135 and LDHB analysis detected 57% of HCC, outperforming the alpha-fetoprotein (AFP) test's sensitivity of 45% at comparable specificity. Furthermore, when used with the AFP test, the methylation assay can detect 70% of HCC. Our findings suggest that the cfDNA methylation assay could be used for HCC liquid biopsy.

Keywords: Biomarker; Cancer diagnosis; Cell-free DNA; DNA methylation.; Hepatocellular carcinoma; Liquid biopsy; Methylation-sensitive high-resolution melting analysis.

Publication types

  • Letter
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Biomarkers, Tumor / genetics
  • Biomarkers, Tumor / metabolism
  • Carcinoma, Hepatocellular* / diagnosis
  • Carcinoma, Hepatocellular* / genetics
  • Carcinoma, Hepatocellular* / pathology
  • Cell-Free Nucleic Acids* / genetics
  • DNA Methylation
  • Humans
  • Liver Neoplasms* / diagnosis
  • Liver Neoplasms* / genetics
  • Liver Neoplasms* / pathology
  • Ubiquitin-Protein Ligases / metabolism
  • alpha-Fetoproteins / analysis
  • alpha-Fetoproteins / genetics
  • alpha-Fetoproteins / metabolism

Substances

  • alpha-Fetoproteins
  • Biomarkers, Tumor
  • Cell-Free Nucleic Acids
  • RNF135 protein, human
  • Ubiquitin-Protein Ligases