Optimization of Ketobenzothiazole-Based Type II Transmembrane Serine Protease Inhibitors to Block H1N1 Influenza Virus Replication

ChemMedChem. 2024 Jan 15;19(2):e202300458. doi: 10.1002/cmdc.202300458. Epub 2023 Oct 31.

Abstract

Human influenza viruses cause acute respiratory symptoms that can lead to death. Due to the emergence of antiviral drug-resistant strains, there is an urgent requirement for novel antiviral agents and innovative therapeutic strategies. Using the peptidomimetic ketobenzothiazole protease inhibitor RQAR-Kbt (IN-1, aka N-0100) as a starting point, we report how substituting P2 and P4 positions with natural and unnatural amino acids can modulate the inhibition potency toward matriptase, a prototypical type II transmembrane serine protease (TTSP) that acts as a priming protease for influenza viruses. We also introduced modifications of the peptidomimetics N-terminal groups, leading to significant improvements (from μM to nM, 60 times more potent than IN-1) in their ability to inhibit the replication of influenza H1N1 virus in the Calu-3 cell line derived from human lungs. The selectivity towards other proteases has been evaluated and explained using molecular modeling with a crystal structure recently obtained by our group. By targeting host cell TTSPs as a therapeutic approach, it may be possible to overcome the high mutational rate of influenza viruses and consequently prevent potential drug resistance.

Keywords: Antiviral agents; influenza; inhibitors; matriptase; type II transmembrane serine protease (TTSP).

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Humans
  • Influenza A Virus, H1N1 Subtype*
  • Influenza A virus* / physiology
  • Influenza, Human* / drug therapy
  • Protease Inhibitors / pharmacology
  • Serine Proteases / metabolism
  • Serine Proteinase Inhibitors / pharmacology
  • Virus Replication

Substances

  • Serine Proteinase Inhibitors
  • Serine Proteases
  • Protease Inhibitors

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