Elexacaftor/tezacaftor/ivacaftor can rescue pancreatic function in F508del homozygous children

Pediatr Pulmonol. 2024 Mar;59(3):788-790. doi: 10.1002/ppul.26794. Epub 2023 Dec 13.

Nadia Nathan^{1

2}, Guillaume Thouvenin^{1

3}, Béatrice Dubern^{4

5}, Harriet Corvol^{1

3}

¹ Pediatric Pulmonology Department, Reference Center for Rare Lung Diseases RespiRare, Armand Trousseau Hospital, Assistance Publique-Hôpitaux de Paris, Sorbonne Université, Paris, France.
² Inserm UMR_S933, Laboratory of Childhood Genetic Diseases, Paris, France.
³ Centre de recherche Saint Antoine (CRSA), Paris, France.
⁴ Assistance Publique-Hôpitaux de Paris, French Reference Center for Prader-Willi Syndrome and Other Rare Obesities (PRADORT), Paris, France.
⁵ Nutrition and Obesities: Systemic Approaches Research Unit (Nutriomics), Sorbonne Université, INSERM, Paris, France.

No abstract available

Keywords: CFTR modulator; children; cystic fibrosis; elexacaftor/tezacaftor/ivacaftor; pancreatic function.

MeSH terms