The Bespoke Gene Therapy Consortium: facilitating development of AAV gene therapies for rare diseases

Nat Rev Drug Discov. 2024 Mar;23(3):157-158. doi: 10.1038/d41573-024-00020-8.
No abstract available

Publication types

  • News

MeSH terms

  • Dependovirus / genetics
  • Gene Transfer Techniques
  • Genetic Therapy*
  • Genetic Vectors
  • Humans
  • Rare Diseases* / genetics
  • Rare Diseases* / therapy