MSX1+PDGFRAlow limb mesenchyme-like cells as an efficient stem cell source for human cartilage regeneration

Stem Cell Reports. 2024 Mar 12;19(3):399-413. doi: 10.1016/j.stemcr.2024.02.001. Epub 2024 Feb 29.

Abstract

Degenerative bone disorders have a significant impact on global health, and regeneration of articular cartilage remains a challenge. Existing cell therapies using mesenchymal stromal cells (MSCs) have shown limited efficacy, highlighting the necessity for alternative stem cell sources. Here, we have identified and characterized MSX1+ mesenchymal progenitor cells in the developing limb bud with remarkable osteochondral-regenerative and microenvironment-adaptive capabilities. Single-cell sequencing further revealed the presence of two major cell compositions within the MSX1+ cells, where a distinct PDGFRAlow subset retained the strongest osteochondral competency and could efficiently regenerate articular cartilage in vivo. Furthermore, a strategy was developed to generate MSX1+PDGFRAlow limb mesenchyme-like (LML) cells from human pluripotent stem cells that closely resembled their mouse counterparts, which were bipotential in vitro and could directly regenerate damaged cartilage in a mouse injury model. Together, our results indicated that MSX1+PDGFRAlow LML cells might be a prominent stem cell source for human cartilage regeneration.

Keywords: MSX1; PDGFRA; cartilage; differentiation; hPSC; in vivo; limb bud-like cells; regeneration.

MeSH terms

  • Animals
  • Cartilage, Articular*
  • Cell Differentiation
  • Cell- and Tissue-Based Therapy
  • Humans
  • MSX1 Transcription Factor / genetics
  • Mesenchymal Stem Cell Transplantation* / methods
  • Mesenchymal Stem Cells*
  • Mesoderm
  • Mice
  • Stem Cells

Substances

  • MSX1 protein, human
  • MSX1 Transcription Factor