Genetic-based patient stratification in Alzheimer's disease

Sci Rep. 2024 Apr 30;14(1):9970. doi: 10.1038/s41598-024-60707-1.

Abstract

Alzheimer's disease (AD) shows a high pathological and symptomatological heterogeneity. To study this heterogeneity, we have developed a patient stratification technique based on one of the most significant risk factors for the development of AD: genetics. We addressed this challenge by including network biology concepts, mapping genetic variants data into a brain-specific protein-protein interaction (PPI) network, and obtaining individualized PPI scores that we then used as input for a clustering technique. We then phenotyped each obtained cluster regarding genetics, sociodemographics, biomarkers, fluorodeoxyglucose-positron emission tomography (FDG-PET) imaging, and neurocognitive assessments. We found three clusters defined mainly by genetic variants found in MAPT, APP, and APOE, considering known variants associated with AD and other neurodegenerative disease genetic architectures. Profiling of these clusters revealed minimal variation in AD symptoms and pathology, suggesting different biological mechanisms may activate the neurodegeneration and pathobiological patterns behind AD and result in similar clinical and pathological presentations, even a shared disease diagnosis. Lastly, our research highlighted MAPT, APP, and APOE as key genes where these genetic distinctions manifest, suggesting them as potential targets for personalized drug development strategies to address each AD subgroup individually.

Publication types

  • Research Support, Non-U.S. Gov't
  • Research Support, N.I.H., Extramural

MeSH terms

  • Aged
  • Alzheimer Disease* / diagnostic imaging
  • Alzheimer Disease* / genetics
  • Amyloid beta-Protein Precursor / genetics
  • Apolipoproteins E* / genetics
  • Biomarkers
  • Brain / diagnostic imaging
  • Brain / metabolism
  • Brain / pathology
  • Female
  • Genetic Predisposition to Disease
  • Humans
  • Male
  • Positron-Emission Tomography*
  • Protein Interaction Maps / genetics
  • tau Proteins* / genetics

Substances

  • tau Proteins
  • Apolipoproteins E
  • MAPT protein, human
  • Amyloid beta-Protein Precursor
  • Biomarkers
  • ApoE protein, human
  • APP protein, human