A persistent variant telomere sequence in a human pedigree

Nat Commun. 2024 Jun 1;15(1):4681. doi: 10.1038/s41467-024-49072-9.

Abstract

The telomere sequence, TTAGGG, is conserved across all vertebrates and plays an essential role in suppressing the DNA damage response by binding a set of proteins termed shelterin. Changes in the telomere sequence impair shelterin binding, initiate a DNA damage response, and are toxic to cells. Here we identify a family with a variant in the telomere template sequence of telomerase, the enzyme responsible for telomere elongation, that led to a non-canonical telomere sequence. The variant is inherited across at least one generation and one family member reports no significant medical concerns despite ~9% of their telomeres converting to the novel sequence. The variant template disrupts telomerase repeat addition processivity and decreased the binding of the telomere-binding protein POT1. Despite these disruptions, the sequence is readily incorporated into cellular chromosomes. Incorporation of a variant sequence prevents POT1-mediated inhibition of telomerase suggesting that incorporation of a variant sequence may influence telomere addition. These findings demonstrate that telomeres can tolerate substantial degeneracy while remaining functional and provide insights as to how incorporation of a non-canonical telomere sequence might alter telomere length dynamics.

MeSH terms

  • Adult
  • Base Sequence
  • Female
  • Humans
  • Male
  • Pedigree*
  • Shelterin Complex* / metabolism
  • Telomerase* / genetics
  • Telomerase* / metabolism
  • Telomere Homeostasis / genetics
  • Telomere* / genetics
  • Telomere* / metabolism
  • Telomere-Binding Proteins* / genetics
  • Telomere-Binding Proteins* / metabolism

Substances

  • Telomere-Binding Proteins
  • Shelterin Complex
  • POT1 protein, human
  • Telomerase