1 Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center, Torrance, CA, USA. lpolgreen@lundquist.org.
2 Department of Pediatrics, David Geffen School of Medicine, University of California, Los Angeles, Los Angeles, CA, USA. lpolgreen@lundquist.org.
3 Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center, Torrance, CA, USA.
4 Department of Pediatrics, David Geffen School of Medicine, University of California, Los Angeles, Los Angeles, CA, USA.
5 Department of Neurology, David Geffen School of Medicine, Brain Research Institute and Molecular Biology Institute University of California, Los Angeles, Los Angeles, CA, USA.
6 Cure Sanfilippo Foundation, Columbia, SC, USA.
7 Department of Pediatrics, University of Minnesota Medical School, Minneapolis, MN, USA.