BTK inhibitors: moving the needle on the treatment of chronic lymphocytic leukemia

Expert Rev Hematol. 2024 Oct;17(10):687-703. doi: 10.1080/17474086.2024.2391097. Epub 2024 Aug 21.

Abstract

Introduction: Bruton's tyrosine kinaseinhibitors (BTKis) changed the trajectory of upfront and relapsed/refractory chronic lymphocytic leukemia (CLL) treatment. However, BTKis are plagued by a spectrum of toxicities. Zanubrutinib was developed to circumvent challenges with prolonged tolerability by increasing BTK selectivity and maximizing efficacy through pharmacokinetic/pharmacodynamic optimization. However, with the availability of ibrutinib, acalabrutinib, and zanubrutinib, limited data exists to guide sequencing of BTKi therapy in the relapsed/refractory setting.

Areas covered: We review the first head-to-head trial (ALPINE) of zanubrutinib versus ibrutinib for the treatment of relapsed/refractory CLL and compare zanubrutinib's clinical efficacy and toxicities, including in patients with del(17p) and/or TP53 mutations to ibrutinib and acalabrutinib.

Expert opinion: Zanubrutinibrepresents one of the new standards of care for relapsed/refractory CLL based on superior progression-free survival and response rates over ibrutinib. Whilezanubrutinib is associated with fewer cardiac toxicities, similar rates of neutropenia and hypertension are noted. Ongoing studies are pushing the envelope, utilizing targeted drug combinations and minimal residual disease markers as well as receptor tyrosine kinase-like orphan receptor 1 inhibitors, chimeric antigen receptor T-cells, and novel BTK degraders. However, zanubrutinibrepresents a strong contender in the arsenal of treatment options for relapsed/refractory CLL.

Keywords: ALPINE; BTK inhibitor; Bruton’s tyrosine kinase; chronic lymphocytic leukemia; zanubrutinib.

Publication types

  • Review

MeSH terms

  • Adenine* / analogs & derivatives
  • Adenine* / therapeutic use
  • Agammaglobulinaemia Tyrosine Kinase* / antagonists & inhibitors
  • Antineoplastic Agents / adverse effects
  • Antineoplastic Agents / therapeutic use
  • Benzamides
  • Humans
  • Leukemia, Lymphocytic, Chronic, B-Cell* / drug therapy
  • Mutation
  • Piperidines* / therapeutic use
  • Protein Kinase Inhibitors* / adverse effects
  • Protein Kinase Inhibitors* / therapeutic use
  • Pyrazines
  • Pyrazoles* / adverse effects
  • Pyrazoles* / therapeutic use
  • Pyrimidines* / therapeutic use
  • Treatment Outcome

Substances

  • Agammaglobulinaemia Tyrosine Kinase
  • Protein Kinase Inhibitors
  • zanubrutinib
  • Piperidines
  • Adenine
  • BTK protein, human
  • Pyrazoles
  • ibrutinib
  • Pyrimidines
  • acalabrutinib
  • Antineoplastic Agents
  • Benzamides
  • Pyrazines