The First Fetal Case of Shwachman-Diamond Syndrome Mimicking Vascular Growth Restriction

Pediatr Dev Pathol. 2024 Nov-Dec;27(6):603-607. doi: 10.1177/10935266241272735. Epub 2024 Aug 31.

Abstract

Shwachman-Diamond Syndrome (SDS) is a rare autosomal recessive genetic condition with 90% of cases associated with biallelic pathogenic variants in the Shwachman-Bodian-Diamond Syndrome (SBDS) gene on chromosome 7q.11.21. SDS belongs to ribosomopathies since SBDS gene encodes a protein involved in ribosomal maturation. Its phenotypic postnatal hallmark features include growth delay, bone marrow failure, exocrine pancreatic insufficiency, and skeletal abnormalities. We report a first fetal case of Shwachman-Diamond syndrome and extend its phenotype before birth. The clinical features mimicked vascular growth restriction with FGR and shortened long bones, associated with abnormal Doppler indices. Non-restricted fetal autopsy after termination of pregnancy allowed deep phenotyping disclosing the features of fetal skeletal dysplasia. Post-fetopathological trio exome sequencing identified biallelic pathogenic variants in the SBDS gene. Genotype-phenotype correlations confirmed the diagnosis and enabled an adequate genetic counseling of the parents. Our case is another example of the positive impact of fetal autopsy coupled with post-fetopathological genomic studies, even in the cases that were hitherto classified as maternal or fetal vascular malperfusion.

Keywords: IUGR; Shwachman-Diamond syndrome (SBDS); placental histology; placental vascular malperfusion; prenatal exome sequencing; ribosomes; whole-exome sequencing.

Publication types

  • Case Reports

MeSH terms

  • Diagnosis, Differential
  • Female
  • Fetal Growth Retardation / diagnosis
  • Fetal Growth Retardation / genetics
  • Fetus
  • Humans
  • Phenotype
  • Pregnancy
  • Proteins
  • Shwachman-Diamond Syndrome*

Substances

  • SBDS protein, human
  • Proteins