Discovery and Preclinical Profile of ALG-055009, a Potent and Selective Thyroid Hormone Receptor Beta (THR-β) Agonist for the Treatment of MASH

J Med Chem. 2024 Sep 12;67(17):14840-14851. doi: 10.1021/acs.jmedchem.4c01029. Epub 2024 Sep 2.

Abstract

Agonists of thyroid hormone receptor β (THR-β) decreased LDL cholesterol (LDL-C) and triglyceride (TG) levels in human clinical trials for patients with dyslipidemia. The authors present the highly potent and selective compound ALG-055009 (14) as a potential best in class THR-β agonist. The high metabolic stability and good permeability translated well in vivo to afford a long in vivo half-life pharmacokinetic profile with limited liability for DDI, and it overcomes certain drawbacks seen in recent clinical candidates.

MeSH terms

  • Animals
  • Drug Discovery
  • Half-Life
  • Humans
  • Male
  • Mice
  • Rats
  • Structure-Activity Relationship
  • Thyroid Hormone Receptors beta* / agonists
  • Thyroid Hormone Receptors beta* / metabolism

Substances

  • Thyroid Hormone Receptors beta