Treating the Untreatable: Antisense Oligonucleotides as an Individualized Therapy for Rare Genetic Kidney Diseases
J Am Soc Nephrol
.
2024 Sep 27.
doi: 10.1681/ASN.0000000532.
Online ahead of print.
Authors
Cedrik Tekendo-Ngongang
1
,
Joseph G Gleeson
1
2
3
,
Laurence Mignon
1
Affiliations
1
n-Lorem Foundation, San Diego, California.
2
Rady Children's Institute for Genomic Medicine, San Diego, California.
3
Department of Neuroscience, University of California, San Diego, California.
PMID:
39331470
DOI:
10.1681/ASN.0000000532
No abstract available
Associated data
ClinicalTrials.gov/NCT04014335
ClinicalTrials.gov/NCT05797610
ClinicalTrials.gov/NCT03070782
ClinicalTrials.gov/NCT00836225
ClinicalTrials.gov/NCT05521191