NEJM at AHA - Phase 1 Study of AAV9.LAMP2B Gene Therapy in Danon Disease
N Engl J Med
.
2024 Nov 18.
doi: 10.1056/NEJMe2414477.
Online ahead of print.
Authors
Eric J Rubin
,
Jane Leopold
,
Stephen Morrissey
PMID:
39555782
DOI:
10.1056/NEJMe2414477
No abstract available
Publication types
Editorial