Gene therapy in heart disease

Adv Exp Med Biol. 1995:369:79-88. doi: 10.1007/978-1-4615-1957-7_8.

Abstract

As the technology for gene therapy develops in vitro and in vivo in animal models, it is becoming clear that the three principal approaches--recombinant retroviruses, recombinant adenovirus, and direct DNA delivery--will ultimately have applications in specific therapeutic situations that take full advantage of the unique features of the specific delivery system: low level persistent expression after ex vivo recombinant retroviral therapy, high level transient expression after in vivo recombinant adenoviral therapy, or moderate level transient expression after in vivo administration of a synthetic DNA complex, which in principle could be repeated as desired.

Publication types

  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, P.H.S.
  • Review

MeSH terms

  • Animals
  • Biological Transport, Active
  • DNA, Recombinant / administration & dosage
  • DNA, Recombinant / genetics
  • Endosomes / metabolism
  • Genetic Therapy* / methods
  • Genetic Vectors
  • Heart Diseases / genetics
  • Heart Diseases / metabolism
  • Heart Diseases / therapy*
  • Humans
  • In Vitro Techniques
  • Orthomyxoviridae / genetics
  • Receptors, LDL / deficiency
  • Receptors, LDL / genetics

Substances

  • DNA, Recombinant
  • Receptors, LDL