Mutations within the FLR exon of NF1 are rare in myelodysplastic syndromes and acute myelocytic leukemias

Leukemia. 1993 Jul;7(7):1058-60.

Abstract

A mutational hotspot in the neurofibromatosis 1 (NF1) gene has recently emerged from the analysis of different malignancies including one patient with myelodysplastic syndrome (MDS). In these cases, Lys 1423 in the GTPase-activating protein (GAP)-related domain of NF1 is substituted which causes a significant reduction of intrinsic GAP activity. We studied 57 MDS patients and 27 cases of acute myelocytic leukemia (AML) for mutations at codon 1423 in the so-called FLR exon of NF1 by an assay based on restriction enzyme digestion. We investigated the entire FLR exon and its flanking intron sequences using single-strand conformation polymorphism (SSCP) analysis of polymerase chain reaction (PCR) products and sequencing. None of the cases exhibited a codon 1423 mutation. However, a patient with chronic myelomonocytic leukemia (CMML) showed a 3 bp deletion within the splice acceptor region in front of the FLR exon. These data suggest that NF1 exon FLR mutations contribute infrequently to the development of MDS and AML.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Acute Disease
  • Base Sequence
  • DNA, Neoplasm / genetics
  • Genes, Neurofibromatosis 1*
  • Humans
  • Leukemia, Myeloid / genetics*
  • Molecular Sequence Data
  • Mutation
  • Myelodysplastic Syndromes / genetics*
  • Oligodeoxyribonucleotides / chemistry

Substances

  • DNA, Neoplasm
  • Oligodeoxyribonucleotides