Molecular diagnosis of hemophilia A in Chinese patients by an analysis of inversions in the factor VIII gene

Hematopathol Mol Hematol. 1996;10(1-2):63-7.

Abstract

Hemophilia A is an X-linked bleeding disorder caused by deleterious mutations in the factor VIII gene. An inversion caused by introchromosomal homologous recombination between the A gene located in intron 22 of the factor VIII gene and one of the two telomeric A genes has been recently described as the common cause of about 50% of cases of severe hemophilia A. The rearrangement can be readily detected by a Southern blotting procedure. We report use of this procedure to detect rearrangements in 106 unrelated Chinese hemophilia A cases. In 49.3% of the patients with severe disease an inversion was found, but no inversion was detected in any of the patients with moderate or mild disease. The majority of inversions (91.4%) involved the most distal A gene; in a minority (8.6%) the more proximal A gene was involved. These results indicate that intron 22 inversion is the most important molecular defect causing Chinese hemophilia A and that analysis for intron 22 inversion may be the first-line test in the molecular diagnosis of severe hemophilia A.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Asian People / genetics*
  • Blotting, Southern
  • China
  • Chromosome Inversion*
  • Factor VIII / genetics*
  • Gene Rearrangement
  • Genetic Testing / methods*
  • Hemophilia A / diagnosis*
  • Hemophilia A / genetics
  • Humans
  • Male

Substances

  • Factor VIII