[Lysinuric dibasic protein intolerance: characteristic aspects of bone marrow involvement]

Arch Pediatr. 1996 Sep;3(9):877-80. doi: 10.1016/0929-693x(96)87577-4.
[Article in French]

Abstract

Background: The marrows of patients with lysinuric protein intolerance (LPI) are generally considered as normal, even though autoerythrophagocytosis has been observed in some of them.

Case reports: Lysinuric protein intolerance was recognized in two 12 and 15-year-old brothers who had been diagnosed following an immuno-hematological investigation. Clinical history had been characterized by a neonatal macrophage activation syndrome (hepatosplenomegaly, pancytopenia, hypofibrinogenemia and hypertriglyceridemia). A putative diagnosis of familial lymphohistiocytosis had been ruled out because of unusual clinical and immunological course. Both brothers had displayed chronic aversion to high-protein foods, failure to thrive, osteoporosis and developmental delay. Metabolic investigations had revealed chronic hyperammonemia while cationic aminoaciduria (lysine, arginine and ornithine) was only present during L-citrulline supplementation. Bone marrow examinations had been performed during the neonatal period and during later metabolic investigations. They both displayed a peculiar red cell and granulocytes phagocytosis by histiocytes and granulocytes precursors.

Conclusions: This aspect of bone marrow could be considered as a specific sign of LPI. This report suggests that appropriate metabolic investigations should be performed in any unexplained macrophage activation syndrome.

Publication types

  • Case Reports
  • English Abstract

MeSH terms

  • Amino Acid Metabolism, Inborn Errors / diagnosis*
  • Bone Marrow / pathology*
  • Follow-Up Studies
  • Humans
  • Infant, Newborn
  • Lysine / metabolism*
  • Macrophage Activation
  • Male

Substances

  • Lysine