Ziegler RJ - Search Results

1

AAV8-mediated hepatic expression of acid sphingomyelinase corrects the metabolic defect in the visceral organs of a mouse model of Niemann-Pick disease.

Barbon CM, Ziegler RJ, Li C, Armentano D, Cherry M, Desnick RJ, Schuchman EH, Cheng SH. Barbon CM, et al. Among authors: ziegler rj. Mol Ther. 2005 Sep;12(3):431-40. doi: 10.1016/j.ymthe.2005.03.011. Mol Ther. 2005. PMID: 16099409 Free article.

2

Adeno-associated virus-mediated expression of acid sphingomyelinase decreases atherosclerotic lesion formation in apolipoprotein E(-/-) mice.

Leger AJ, Mosquea LM, Li L, Chuang W, Pacheco J, Taylor K, Luo Z, Piepenhagen P, Ziegler R, Moreland R, Urabe A, Jiang C, Cheng SH, Yew NS. Leger AJ, et al. J Gene Med. 2011 Jun;13(6):324-32. doi: 10.1002/jgm.1575. J Gene Med. 2011. PMID: 21674735

3

Adenovirus-transduced lung as a portal for delivering alpha-galactosidase A into systemic circulation for Fabry disease.

Li C, Ziegler RJ, Cherry M, Lukason M, Desnick RJ, Yew NS, Cheng SH. Li C, et al. Among authors: ziegler rj. Mol Ther. 2002 Jun;5(6):745-54. doi: 10.1006/mthe.2002.0605. Mol Ther. 2002. PMID: 12027559 Free article.

4

Correction of the nonlinear dose response improves the viability of adenoviral vectors for gene therapy of Fabry disease.

Ziegler RJ, Li C, Cherry M, Zhu Y, Hempel D, van Rooijen N, Ioannou YA, Desnick RJ, Goldberg MA, Yew NS, Cheng SH. Ziegler RJ, et al. Hum Gene Ther. 2002 May 20;13(8):935-45. doi: 10.1089/10430340252939041. Hum Gene Ther. 2002. PMID: 12031126

5

Demonstration of feasibility of in vivo gene therapy for Gaucher disease using a chemically induced mouse model.

Marshall J, McEachern KA, Kyros JA, Nietupski JB, Budzinski T, Ziegler RJ, Yew NS, Sullivan J, Scaria A, van Rooijen N, Barranger JA, Cheng SH. Marshall J, et al. Among authors: ziegler rj. Mol Ther. 2002 Aug;6(2):179-89. doi: 10.1006/mthe.2002.0650. Mol Ther. 2002. PMID: 12161184 Free article.

6

Partial correction of the alpha-galactosidase A deficiency and reduction of glycolipid storage in Fabry mice using synthetic vectors.

Przybylska M, Wu IH, Zhao H, Ziegler RJ, Tousignant JD, Desnick RJ, Scheule RK, Cheng SH, Yew NS. Przybylska M, et al. Among authors: ziegler rj. J Gene Med. 2004 Jan;6(1):85-92. doi: 10.1002/jgm.468. J Gene Med. 2004. PMID: 14716680

7

AAV2 vector harboring a liver-restricted promoter facilitates sustained expression of therapeutic levels of alpha-galactosidase A and the induction of immune tolerance in Fabry mice.

Ziegler RJ, Lonning SM, Armentano D, Li C, Souza DW, Cherry M, Ford C, Barbon CM, Desnick RJ, Gao G, Wilson JM, Peluso R, Godwin S, Carter BJ, Gregory RJ, Wadsworth SC, Cheng SH. Ziegler RJ, et al. Mol Ther. 2004 Feb;9(2):231-40. doi: 10.1016/j.ymthe.2003.11.015. Mol Ther. 2004. PMID: 14759807 Free article.

8

Correction of the biochemical and functional deficits in fabry mice following AAV8-mediated hepatic expression of alpha-galactosidase A.

Ziegler RJ, Cherry M, Barbon CM, Li C, Bercury SD, Armentano D, Desnick RJ, Cheng SH. Ziegler RJ, et al. Mol Ther. 2007 Mar;15(3):492-500. doi: 10.1038/sj.mt.6300066. Epub 2006 Dec 26. Mol Ther. 2007. PMID: 17191071 Free article.

9

Combination brain and systemic injections of AAV provide maximal functional and survival benefits in the Niemann-Pick mouse.

Passini MA, Bu J, Fidler JA, Ziegler RJ, Foley JW, Dodge JC, Yang WW, Clarke J, Taksir TV, Griffiths DA, Zhao MA, O'Riordan CR, Schuchman EH, Shihabuddin LS, Cheng SH. Passini MA, et al. Among authors: ziegler rj. Proc Natl Acad Sci U S A. 2007 May 29;104(22):9505-10. doi: 10.1073/pnas.0703509104. Epub 2007 May 21. Proc Natl Acad Sci U S A. 2007. PMID: 17517638 Free PMC article.

10

Ability of adeno-associated virus serotype 8-mediated hepatic expression of acid alpha-glucosidase to correct the biochemical and motor function deficits of presymptomatic and symptomatic Pompe mice.

Ziegler RJ, Bercury SD, Fidler J, Zhao MA, Foley J, Taksir TV, Ryan S, Hodges BL, Scheule RK, Shihabuddin LS, Cheng SH. Ziegler RJ, et al. Hum Gene Ther. 2008 Jun;19(6):609-21. doi: 10.1089/hum.2008.010. Hum Gene Ther. 2008. PMID: 18500944

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