Sevin C - Search Results

1

Gene therapy in metachromatic leukodystrophy.

Sevin C, Cartier-Lacave N, Aubourg P. Sevin C, et al. Int J Clin Pharmacol Ther. 2009;47 Suppl 1:S128-31. doi: 10.5414/cpp47128. Int J Clin Pharmacol Ther. 2009. PMID: 20040324 Review.

2

Intracerebral adeno-associated virus-mediated gene transfer in rapidly progressive forms of metachromatic leukodystrophy.

Sevin C, Benraiss A, Van Dam D, Bonnin D, Nagels G, Verot L, Laurendeau I, Vidaud M, Gieselmann V, Vanier M, De Deyn PP, Aubourg P, Cartier N. Sevin C, et al. Hum Mol Genet. 2006 Jan 1;15(1):53-64. doi: 10.1093/hmg/ddi425. Epub 2005 Nov 25. Hum Mol Genet. 2006. PMID: 16311251

3

Partial cure of established disease in an animal model of metachromatic leukodystrophy after intracerebral adeno-associated virus-mediated gene transfer.

Sevin C, Verot L, Benraiss A, Van Dam D, Bonnin D, Nagels G, Fouquet F, Gieselmann V, Vanier MT, De Deyn PP, Aubourg P, Cartier N. Sevin C, et al. Gene Ther. 2007 Mar;14(5):405-14. doi: 10.1038/sj.gt.3302883. Epub 2006 Nov 9. Gene Ther. 2007. PMID: 17093507

4

Enzyme, cell and gene-based therapies for metachromatic leukodystrophy.

Sevin C, Aubourg P, Cartier N. Sevin C, et al. J Inherit Metab Dis. 2007 Apr;30(2):175-83. doi: 10.1007/s10545-007-0540-z. Epub 2007 Mar 8. J Inherit Metab Dis. 2007. PMID: 17347913 Review.

5

Efficient intracerebral delivery of AAV5 vector encoding human ARSA in non-human primate.

Colle MA, Piguet F, Bertrand L, Raoul S, Bieche I, Dubreil L, Sloothaak D, Bouquet C, Moullier P, Aubourg P, Cherel Y, Cartier N, Sevin C. Colle MA, et al. Among authors: sevin c. Hum Mol Genet. 2010 Jan 1;19(1):147-58. doi: 10.1093/hmg/ddp475. Hum Mol Genet. 2010. PMID: 19837699

6

Autosomal recessive cerebellar ataxia caused by mutations in the PEX2 gene.

Sevin C, Ferdinandusse S, Waterham HR, Wanders RJ, Aubourg P. Sevin C, et al. Orphanet J Rare Dis. 2011 Mar 10;6:8. doi: 10.1186/1750-1172-6-8. Orphanet J Rare Dis. 2011. PMID: 21392394 Free PMC article.

7

Toward a better understanding of brain lesions during metachromatic leukodystrophy evolution.

Martin A, Sevin C, Lazarus C, Bellesme C, Aubourg P, Adamsbaum C. Martin A, et al. Among authors: sevin c. AJNR Am J Neuroradiol. 2012 Oct;33(9):1731-9. doi: 10.3174/ajnr.A3038. Epub 2012 Apr 26. AJNR Am J Neuroradiol. 2012. PMID: 22538069 Free PMC article.

8

Correction of brain oligodendrocytes by AAVrh.10 intracerebral gene therapy in metachromatic leukodystrophy mice.

Piguet F, Sondhi D, Piraud M, Fouquet F, Hackett NR, Ahouansou O, Vanier MT, Bieche I, Aubourg P, Crystal RG, Cartier N, Sevin C. Piguet F, et al. Among authors: sevin c. Hum Gene Ther. 2012 Aug;23(8):903-14. doi: 10.1089/hum.2012.015. Epub 2012 Jul 23. Hum Gene Ther. 2012. PMID: 22642214 Free PMC article.

9

Comparative efficacy and safety of multiple routes of direct CNS administration of adeno-associated virus gene transfer vector serotype rh.10 expressing the human arylsulfatase A cDNA to nonhuman primates.

Rosenberg JB, Sondhi D, Rubin DG, Monette S, Chen A, Cram S, De BP, Kaminsky SM, Sevin C, Aubourg P, Crystal RG. Rosenberg JB, et al. Among authors: sevin c. Hum Gene Ther Clin Dev. 2014 Sep;25(3):164-77. doi: 10.1089/humc.2013.239. Epub 2014 Aug 21. Hum Gene Ther Clin Dev. 2014. PMID: 25144894 Free PMC article.

10

Intracerebral Gene Therapy Using AAVrh.10-hARSA Recombinant Vector to Treat Patients with Early-Onset Forms of Metachromatic Leukodystrophy: Preclinical Feasibility and Safety Assessments in Nonhuman Primates.

Zerah M, Piguet F, Colle MA, Raoul S, Deschamps JY, Deniaud J, Gautier B, Toulgoat F, Bieche I, Laurendeau I, Sondhi D, Souweidane MM, Cartier-Lacave N, Moullier P, Crystal RG, Roujeau T, Sevin C, Aubourg P. Zerah M, et al. Among authors: sevin c. Hum Gene Ther Clin Dev. 2015 Jun;26(2):113-24. doi: 10.1089/humc.2014.139. Epub 2015 Apr 28. Hum Gene Ther Clin Dev. 2015. PMID: 25758611 Clinical Trial.

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