Elexacaftor/tezacaftor/ivacaftor efficacy in intestinal organoids with rare CFTR variants in comparison to CFTR-F508del and CFTR-wild type controls.
Kroes S, Bierlaagh MC, Lefferts JW, Boni A, Muilwijk D, Viscomi C, Keijzer-Nieuwenhuijze NDA, Cristiani L, Niemöller PJ, Verburg TF, Cutrera R, Fiocchi AG, Lucidi V, van der Ent CK, Beekman JM, Alghisi F, Ciciriello F.
Kroes S, et al. Among authors: van der ent ck.
J Cyst Fibros. 2024 Nov 9:S1569-1993(24)01787-9. doi: 10.1016/j.jcf.2024.09.019. Online ahead of print.
J Cyst Fibros. 2024.
PMID: 39523185