Effects of nusinersen after one year of treatment in 123 children with SMA type 1 or 2: a French real-life observational study.
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Audic F, et al. Among authors: cuisset jm.
Orphanet J Rare Dis. 2020 Jun 12;15(1):148. doi: 10.1186/s13023-020-01414-8.
Orphanet J Rare Dis. 2020.
PMID: 32532349
Free PMC article.